Spinraza, INN - nusinersen
nusinersen | Ligand page | IUPHAR/BPS Guide to PHARMACOLOGY
Discovery of a CNS penetrant small molecule SMN2 splicing modulator with improved tolerability for spinal muscular atrophy | Scientific Reports
Quality of Life in SMA Patients Under Treatment With Nusinersen
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Nusinersen - Wikipedia
Therapy development for spinal muscular atrophy: perspectives for muscular dystrophies and neurodegenerative disorders | Neurological Research and Practice | Full Text
Antisense oligonucleotides (ASOs) in clinical use. (A) Nusinersen binds... | Download Scientific Diagram
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
Nusinersen - an overview | ScienceDirect Topics
How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy | Gene Therapy
Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy: Molecular Therapy - Nucleic Acids
FN170919 | 1258984-36-9 | Nusinersen | Biosynth
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Medicina | Free Full-Text | The Safety and Efficacy of Nusinersen in the Treatment of Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis of Randomized Controlled Trials
IJMS | Free Full-Text | Nusinersen Modulates Proteomics Profiles of Cerebrospinal Fluid in Spinal Muscular Atrophy Type 1 Patients
nusinersen | Ligand page | IUPHAR/BPS Guide to PHARMACOLOGY
Nusinersen ameliorates motor function and prevents motoneuron Cajal body disassembly and abnormal poly(A) RNA distribution in a SMA mouse model | Scientific Reports
Nusinersen in the Treatment of Spinal Muscular Atrophy | SpringerLink
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
SPINRAZA (nusinersen) injection, for intrathecal use
CSF and plasma concentrations of nusinersen | Download Scientific Diagram
