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Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development
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Low-density lipoprotein receptor-deficient hepatocytes differentiated from induced pluripotent stem cells allow familial hypercholesterolemia modeling, CRISPR/Cas-mediated genetic correction, and productive hepatitis C virus infection | Stem Cell ...
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Engineering the AAVS1 locus for consistent and scalable transgene expression in human iPSCs and their differentiated derivatives - ScienceDirect
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An AAVS1-Targeted Minigene Platform for Correction of iPSCs From All Five Types of Chronic Granulomatous Disease: Molecular Therapy
Identification of the safe harbor locus, AAVS1, from porcine genome and site-specific integration of recombinase-mediated casset
![a). Schematic of the AAVS1 locus and the AAV-CAGGS-GFP donor plasmid... | Download Scientific Diagram a). Schematic of the AAVS1 locus and the AAV-CAGGS-GFP donor plasmid... | Download Scientific Diagram](https://www.researchgate.net/publication/255694391/figure/fig3/AS:214256827015175@1428094216323/a-Schematic-of-the-AAVS1-locus-and-the-AAV-CAGGS-GFP-donor-plasmid-with-homology-arms.png)
a). Schematic of the AAVS1 locus and the AAV-CAGGS-GFP donor plasmid... | Download Scientific Diagram
![A) Nucleotide sequence alignment of the human, mouse, and monkey AAVS1... | Download Scientific Diagram A) Nucleotide sequence alignment of the human, mouse, and monkey AAVS1... | Download Scientific Diagram](https://www.researchgate.net/publication/8428486/figure/fig1/AS:281054976987136@1444020136037/A-Nucleotide-sequence-alignment-of-the-human-mouse-and-monkey-AAVS1-sequences.png)
A) Nucleotide sequence alignment of the human, mouse, and monkey AAVS1... | Download Scientific Diagram
![Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development](https://www.cell.com/cms/attachment/60d4043d-d0b9-4d06-af20-f75553f034de/gr1_lrg.jpg)
Quantification of transgene expression in GSH AAVS1 with a novel CRISPR/Cas9-based approach reveals high transcriptional variation: Molecular Therapy - Methods & Clinical Development
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